Gene therapy to cure haemophilia: Is robust scientific inquiry the missing factor?

Haemophilia. 2020 Nov;26(6):931-933. doi: 10.1111/hae.14131. Epub 2020 Sep 10.

Authors

Glenn F Pierce¹, Radoslaw Kaczmarek², Declan Noone³, Brian O'Mahony⁴, David Page⁵, Mark W Skinner⁶

Affiliations

¹ World Federation of Hemophilia, Montreal, QC, Canada.
² Polish Hemophilia Society, Warsaw, Poland.
³ European Haemophilia Consortium, Brussels, Belgium.
⁴ Irish Haemophilia Society, Dublin, Ireland.
⁵ Canadian Haemophilia Society, Montreal, Canada.
⁶ National Hemophilia Foundation, New York, NY, USA.

PMID: 32909632
DOI: 10.1111/hae.14131

No abstract available

MeSH terms

Genetic Therapy
Hemophilia A / genetics*
Hemophilia A / therapy*
Humans