Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I.
Clarke LA, Wraith JE, Beck M, Kolodny EH, Pastores GM, Muenzer J, Rapoport DM, Berger KI, Sidman M, Kakkis ED, Cox GF.
Clarke LA, et al. Among authors: kolodny eh.
Pediatrics. 2009 Jan;123(1):229-40. doi: 10.1542/peds.2007-3847.
Pediatrics. 2009.
PMID: 19117887
Clinical Trial.