Cognitive function in SMA patients with 2 or 3 SMN2 copies treated with SMN-modifying or gene addition therapy during the first year of life.
Steffens P, Weiss D, Perez A, Appel M, Weber P, Weiss C, Stoltenburg C, Ehinger U, von der Hagen M, Schallner J, Claussen B, Lode I, Hahn A, Schuler R, Ruß L, Ziegler A, Denecke J, Johannsen J.
Steffens P, et al. Among authors: von der hagen m.
Eur J Paediatr Neurol. 2024 May 8;51:17-23. doi: 10.1016/j.ejpn.2024.05.002. Online ahead of print.
Eur J Paediatr Neurol. 2024.
PMID: 38772209