Gene Therapy for Genetic Syndromes: Understanding the Current State to Guide Future Care.
Henderson ML, Zieba JK, Li X, Campbell DB, Williams MR, Vogt DL, Bupp CP, Edgerly YM, Rajasekaran S, Hartog NL, Prokop JW, Krueger JM.
Henderson ML, et al. Among authors: vogt dl.
BioTech (Basel). 2024 Jan 3;13(1):1. doi: 10.3390/biotech13010001.
BioTech (Basel). 2024.
PMID: 38247731
Free PMC article.
Review.