Pastores GM - Search Results

1

Agalsidase alfa in pediatric patients with Fabry disease: a 6.5-year open-label follow-up study.

Schiffmann R, Pastores GM, Lien YH, Castaneda V, Chang P, Martin R, Wijatyk A. Schiffmann R, et al. Among authors: pastores gm. Orphanet J Rare Dis. 2014 Nov 26;9:169. doi: 10.1186/s13023-014-0169-6. Orphanet J Rare Dis. 2014. PMID: 25425121 Free PMC article. Clinical Trial.

2

Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.

Schiffmann R, Martin RA, Reimschisel T, Johnson K, Castaneda V, Lien YH, Pastores GM, Kampmann C, Ries M, Clarke JT. Schiffmann R, et al. Among authors: pastores gm. J Pediatr. 2010 May;156(5):832-7, 837.e1. doi: 10.1016/j.jpeds.2009.11.007. Epub 2010 Jan 25. J Pediatr. 2010. PMID: 20097359 Clinical Trial.

3

Biochemical and molecular genetic basis of Fabry disease.

Pastores GM, Lien YH. Pastores GM, et al. J Am Soc Nephrol. 2002 Jun;13 Suppl 2:S130-3. J Am Soc Nephrol. 2002. PMID: 12068024 Review. No abstract available.

4

Taliglucerase alfa: safety and efficacy across 6 clinical studies in adults and children with Gaucher disease.

Zimran A, Wajnrajch M, Hernandez B, Pastores GM. Zimran A, et al. Among authors: pastores gm. Orphanet J Rare Dis. 2018 Feb 23;13(1):36. doi: 10.1186/s13023-018-0776-8. Orphanet J Rare Dis. 2018. PMID: 29471850 Free PMC article. Review.

5

Safety and pharmacokinetics of agalsidase alfa in patients with Fabry disease and end-stage renal disease.

Pastores GM, Boyd E, Crandall K, Whelan A, Piersall L, Barnett N. Pastores GM, et al. Nephrol Dial Transplant. 2007 Jul;22(7):1920-5. doi: 10.1093/ndt/gfm096. Epub 2007 Mar 29. Nephrol Dial Transplant. 2007. PMID: 17395657 Clinical Trial.

6

Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources.

Grabowski GA, Barton NW, Pastores G, Dambrosia JM, Banerjee TK, McKee MA, Parker C, Schiffmann R, Hill SC, Brady RO. Grabowski GA, et al. Ann Intern Med. 1995 Jan 1;122(1):33-9. doi: 10.7326/0003-4819-122-1-199501010-00005. Ann Intern Med. 1995. PMID: 7985893 Clinical Trial.

7

A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: safety and tolerability.

Pastores GM, Rosenbloom B, Weinreb N, Goker-Alpan O, Grabowski G, Cohn GM, Zahrieh D. Pastores GM, et al. Genet Med. 2014 May;16(5):359-66. doi: 10.1038/gim.2013.154. Epub 2013 Nov 21. Genet Med. 2014. PMID: 24263462 Free PMC article. Clinical Trial.

8

A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase.

Pastores GM, Petakov M, Giraldo P, Rosenbaum H, Szer J, Deegan PB, Amato DJ, Mengel E, Tan ES, Chertkoff R, Brill-Almon E, Zimran A. Pastores GM, et al. Blood Cells Mol Dis. 2014 Dec;53(4):253-60. doi: 10.1016/j.bcmd.2014.05.004. Epub 2014 Jun 18. Blood Cells Mol Dis. 2014. PMID: 24950666 Clinical Trial.

9

Development of anti-velaglucerase alfa antibodies in clinical trial-treated patients with Gaucher disease.

Pastores GM, Turkia HB, Gonzalez DE, Ida H, Tantawy AA, Qin Y, Qiu Y, Dinh Q, Zimran A. Pastores GM, et al. Blood Cells Mol Dis. 2016 Jul;59:37-43. doi: 10.1016/j.bcmd.2016.03.004. Epub 2016 Mar 5. Blood Cells Mol Dis. 2016. PMID: 27282565 Free article. Clinical Trial.

10

Long-term velaglucerase alfa treatment in children with Gaucher disease type 1 naïve to enzyme replacement therapy or previously treated with imiglucerase.

Smith L, Rhead W, Charrow J, Shankar SP, Bavdekar A, Longo N, Mardach R, Harmatz P, Hangartner T, Lee HM, Crombez E, Pastores GM. Smith L, et al. Among authors: pastores gm. Mol Genet Metab. 2016 Feb;117(2):164-71. doi: 10.1016/j.ymgme.2015.05.012. Epub 2015 Jun 1. Mol Genet Metab. 2016. PMID: 26043810 Free article. Clinical Trial.

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