Mueller C - Search Results

1

Intralingual Administration of AAVrh10-miR^SOD1 Improves Respiratory But Not Swallowing Function in a Superoxide Dismutase-1 Mouse Model of Amyotrophic Lateral Sclerosis.

Lind LA, Andel EM, McCall AL, Dhindsa JS, Johnson KA, Stricklin OE, Mueller C, ElMallah MK, Lever TE, Nichols NL. Lind LA, et al. Among authors: mueller c. Hum Gene Ther. 2020 Aug;31(15-16):828-838. doi: 10.1089/hum.2020.065. Epub 2020 Jul 13. Hum Gene Ther. 2020. PMID: 32498636 Free PMC article.

2

Clinical gene therapy using recombinant adeno-associated virus vectors.

Mueller C, Flotte TR. Mueller C, et al. Gene Ther. 2008 Jun;15(11):858-63. doi: 10.1038/gt.2008.68. Epub 2008 Apr 17. Gene Ther. 2008. PMID: 18418415 Review.

3

Apparently nonspecific enzyme elevations after portal vein delivery of recombinant adeno-associated virus serotype 2 vector in hepatitis C virus-infected chimpanzees.

Flotte TR, Goetzmann J, Caridi J, Paolillo J, Conlon TJ, Potter M, Mueller C, Byrne BJ. Flotte TR, et al. Among authors: mueller c. Hum Gene Ther. 2008 Jul;19(7):681-9. doi: 10.1089/hum.2007.174. Hum Gene Ther. 2008. PMID: 18588426 Free PMC article.

4

The pros and cons of immunomodulatory IL-10 gene therapy with recombinant AAV in a Cftr-/- -dependent allergy mouse model.

Mueller C, Braag SA, Martino AT, Tang Q, Campbell-Thompson M, Flotte TR. Mueller C, et al. Gene Ther. 2009 Feb;16(2):172-83. doi: 10.1038/gt.2008.156. Epub 2008 Sep 25. Gene Ther. 2009. PMID: 18818669

5

Recombinant AAV serotype and capsid mutant comparison for pulmonary gene transfer of alpha-1-antitrypsin using invasive and noninvasive delivery.

Liqun Wang R, McLaughlin T, Cossette T, Tang Q, Foust K, Campbell-Thompson M, Martino A, Cruz P, Loiler S, Mueller C, Flotte TR. Liqun Wang R, et al. Among authors: mueller c. Mol Ther. 2009 Jan;17(1):81-7. doi: 10.1038/mt.2008.217. Epub 2008 Oct 21. Mol Ther. 2009. PMID: 18941444 Free PMC article.

6

In vitro and in vivo functional characterization of gutless recombinant SV40-derived CFTR vectors.

Mueller C, Strayer MS, Sirninger J, Braag S, Branco F, Louboutin JP, Flotte TR, Strayer DS. Mueller C, et al. Gene Ther. 2010 Feb;17(2):227-37. doi: 10.1038/gt.2009.137. Epub 2009 Nov 5. Gene Ther. 2010. PMID: 19890354 Free PMC article.

7

MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression.

Xie J, Xie Q, Zhang H, Ameres SL, Hung JH, Su Q, He R, Mu X, Seher Ahmed S, Park S, Kato H, Li C, Mueller C, Mello CC, Weng Z, Flotte TR, Zamore PD, Gao G. Xie J, et al. Among authors: mueller c. Mol Ther. 2011 Mar;19(3):526-35. doi: 10.1038/mt.2010.279. Epub 2010 Dec 21. Mol Ther. 2011. PMID: 21179009 Free PMC article.

8

Phase 2 clinical trial of a recombinant adeno-associated viral vector expressing α1-antitrypsin: interim results.

Flotte TR, Trapnell BC, Humphries M, Carey B, Calcedo R, Rouhani F, Campbell-Thompson M, Yachnis AT, Sandhaus RA, McElvaney NG, Mueller C, Messina LM, Wilson JM, Brantly M, Knop DR, Ye GJ, Chulay JD. Flotte TR, et al. Among authors: mueller c. Hum Gene Ther. 2011 Oct;22(10):1239-47. doi: 10.1089/hum.2011.053. Epub 2011 Aug 24. Hum Gene Ther. 2011. PMID: 21609134 Free PMC article. Clinical Trial.

9

Several rAAV vectors efficiently cross the blood-brain barrier and transduce neurons and astrocytes in the neonatal mouse central nervous system.

Zhang H, Yang B, Mu X, Ahmed SS, Su Q, He R, Wang H, Mueller C, Sena-Esteves M, Brown R, Xu Z, Gao G. Zhang H, et al. Among authors: mueller c. Mol Ther. 2011 Aug;19(8):1440-8. doi: 10.1038/mt.2011.98. Epub 2011 May 24. Mol Ther. 2011. PMID: 21610699 Free PMC article.

10

Sustained miRNA-mediated knockdown of mutant AAT with simultaneous augmentation of wild-type AAT has minimal effect on global liver miRNA profiles.

Mueller C, Tang Q, Gruntman A, Blomenkamp K, Teckman J, Song L, Zamore PD, Flotte TR. Mueller C, et al. Mol Ther. 2012 Mar;20(3):590-600. doi: 10.1038/mt.2011.292. Epub 2012 Jan 17. Mol Ther. 2012. PMID: 22252449 Free PMC article.

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