Giroctocogene fitelparvovec gene therapy for severe hemophilia A: 104-week analysis of the phase 1/2 Alta study.
Leavitt AD, Konkle BA, Stine KC, Visweshwar N, Harrington TJ, Giermasz A, Arkin S, Fang A, Plonski F, Yver A, Ganne F, Agathon D, Resa MLA, Tseng LJ, Di Russo G, Cockroft BM, Cao L, Rupon J.
Leavitt AD, et al. Among authors: cao l.
Blood. 2024 Feb 29;143(9):796-806. doi: 10.1182/blood.2022018971.
Blood. 2024.
PMID: 37871576
Free PMC article.
Clinical Trial.