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Effect of genistein and coenzyme Q10 in oxidative damage and mitochondrial membrane potential in an attenuated type II mucopolysaccharidosis cellular model.
Cell Biochem Funct. 2024 Mar;42(2):e3932. doi: 10.1002/cbf.3932.
Cell Biochem Funct. 2024.
PMID: 38332678
Characterization of heart disease in mucopolysaccharidosis type II mice.
Tavares AMV, Gonzalez EA, Viana IS, Visioli F, Vera LNP, Baldo G.
Tavares AMV, et al. Among authors: vera lnp.
Cardiovasc Pathol. 2023 Nov-Dec;67:107575. doi: 10.1016/j.carpath.2023.107575. Epub 2023 Sep 18.
Cardiovasc Pathol. 2023.
PMID: 37730078
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CNS Repopulation by Hematopoietic-Derived Microglia-Like Cells Corrects Progranulin deficiency.
Colella P, Sayana R, Suarez-Nieto MV, Sarno J, Nyame K, Xiong J, Vera LNP, Basurto JA, Corbo M, Limaye A, Davis KL, Abu-Remaileh M, Gomez-Ospina N.
Colella P, et al. Among authors: vera lnp.
Res Sq [Preprint]. 2023 Sep 12:rs.3.rs-3263412. doi: 10.21203/rs.3.rs-3263412/v1.
Res Sq. 2023.
PMID: 37790525
Free PMC article.
Preprint.
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Evaluation of oxidative stress and mitochondrial function in a type II mucopolysaccharidosis cellular model: in vitro effects of genistein and coenzyme Q10.
Jacques CED, Lopes FF, Poletto E, Vera LNP, Vianna P, Reinhardt LS, Baldo G, Vargas CR.
Jacques CED, et al. Among authors: vera lnp.
Metab Brain Dis. 2023 Feb;38(2):519-529. doi: 10.1007/s11011-022-01062-w. Epub 2022 Aug 27.
Metab Brain Dis. 2023.
PMID: 36029429
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Brain and visceral gene editing of mucopolysaccharidosis I mice by nasal delivery of the CRISPR/Cas9 system.
Vera LNP, Schuh RS, Fachel FNS, Poletto E, Piovesan E, Kubaski F, Couto E, Brum B, Rodrigues G, Souza H, Giugliani R, Matte U, Baldo G, Teixeira HF.
Vera LNP, et al.
J Gene Med. 2022 Apr;24(4):e3410. doi: 10.1002/jgm.3410. Epub 2022 Jan 31.
J Gene Med. 2022.
PMID: 35032067
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In Situ Gene Therapy.
Santos HS, Rodrigues L, Vera LNP, Poletto E, Filippi-Chiela E, Dos Santos Bruschi LFR, Schuh R, Baldo G.
Santos HS, et al. Among authors: vera lnp.
Curr Gene Ther. 2021;21(5):406-430. doi: 10.2174/1566523221666210504103323.
Curr Gene Ther. 2021.
PMID: 33949931
Review.
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Neonatal nonviral gene editing with the CRISPR/Cas9 system improves some cardiovascular, respiratory, and bone disease features of the mucopolysaccharidosis I phenotype in mice.
Schuh RS, Gonzalez EA, Tavares AMV, Seolin BG, Elias LS, Vera LNP, Kubaski F, Poletto E, Giugliani R, Teixeira HF, Matte U, Baldo G.
Schuh RS, et al. Among authors: vera lnp.
Gene Ther. 2020 Feb;27(1-2):74-84. doi: 10.1038/s41434-019-0113-4. Epub 2019 Dec 11.
Gene Ther. 2020.
PMID: 31827259
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