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Antisense oligonucleotides: treating neurodegeneration at the level of RNA.
Neurotherapeutics. 2013 Jul;10(3):486-97. doi: 10.1007/s13311-013-0194-5.
Neurotherapeutics. 2013.
PMID: 23686823
Free PMC article.
Review.
Method for widespread microRNA-155 inhibition prolongs survival in ALS-model mice.
Koval ED, Shaner C, Zhang P, du Maine X, Fischer K, Tay J, Chau BN, Wu GF, Miller TM.
Koval ED, et al.
Hum Mol Genet. 2013 Oct 15;22(20):4127-35. doi: 10.1093/hmg/ddt261. Epub 2013 Jun 4.
Hum Mol Genet. 2013.
PMID: 23740943
Free PMC article.
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Heparan sulfate proteoglycans mediate internalization and propagation of specific proteopathic seeds.
Holmes BB, DeVos SL, Kfoury N, Li M, Jacks R, Yanamandra K, Ouidja MO, Brodsky FM, Marasa J, Bagchi DP, Kotzbauer PT, Miller TM, Papy-Garcia D, Diamond MI.
Holmes BB, et al.
Proc Natl Acad Sci U S A. 2013 Aug 13;110(33):E3138-47. doi: 10.1073/pnas.1301440110. Epub 2013 Jul 29.
Proc Natl Acad Sci U S A. 2013.
PMID: 23898162
Free PMC article.
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An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study.
Miller TM, Pestronk A, David W, Rothstein J, Simpson E, Appel SH, Andres PL, Mahoney K, Allred P, Alexander K, Ostrow LW, Schoenfeld D, Macklin EA, Norris DA, Manousakis G, Crisp M, Smith R, Bennett CF, Bishop KM, Cudkowicz ME.
Miller TM, et al.
Lancet Neurol. 2013 May;12(5):435-42. doi: 10.1016/S1474-4422(13)70061-9. Epub 2013 Mar 29.
Lancet Neurol. 2013.
PMID: 23541756
Free PMC article.
Clinical Trial.
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Canine degenerative myelopathy: biochemical characterization of superoxide dismutase 1 in the first naturally occurring non-human amyotrophic lateral sclerosis model.
Crisp MJ, Beckett J, Coates JR, Miller TM.
Crisp MJ, et al.
Exp Neurol. 2013 Oct;248:1-9. doi: 10.1016/j.expneurol.2013.05.009. Epub 2013 May 23.
Exp Neurol. 2013.
PMID: 23707216
Free PMC article.
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SOD1 in cerebral spinal fluid as a pharmacodynamic marker for antisense oligonucleotide therapy.
Winer L, Srinivasan D, Chun S, Lacomis D, Jaffa M, Fagan A, Holtzman DM, Wancewicz E, Bennett CF, Bowser R, Cudkowicz M, Miller TM.
Winer L, et al.
JAMA Neurol. 2013 Feb;70(2):201-7. doi: 10.1001/jamaneurol.2013.593.
JAMA Neurol. 2013.
PMID: 23147550
Free PMC article.
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Direct intraventricular delivery of drugs to the rodent central nervous system.
DeVos SL, Miller TM.
DeVos SL, et al.
J Vis Exp. 2013 May 12;(75):e50326. doi: 10.3791/50326.
J Vis Exp. 2013.
PMID: 23712122
Free PMC article.
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