Wraith JE - Search Results

1

Characterization of surgical procedures in patients with mucopolysaccharidosis type I: findings from the MPS I Registry.

Arn P, Wraith JE, Underhill L. Arn P, et al. Among authors: wraith je. J Pediatr. 2009 Jun;154(6):859-64.e3. doi: 10.1016/j.jpeds.2008.12.024. Epub 2009 Feb 12. J Pediatr. 2009. PMID: 19217123

2

High rate of postoperative mortality in patients with mucopolysaccharidosis I: findings from the MPS I Registry.

Arn P, Whitley C, Wraith JE, Webb HW, Underhill L, Rangachari L, Cox GF. Arn P, et al. Among authors: wraith je. J Pediatr Surg. 2012 Mar;47(3):477-84. doi: 10.1016/j.jpedsurg.2011.09.042. J Pediatr Surg. 2012. PMID: 22424341

3

The MPS I registry: design, methodology, and early findings of a global disease registry for monitoring patients with Mucopolysaccharidosis Type I.

Pastores GM, Arn P, Beck M, Clarke JT, Guffon N, Kaplan P, Muenzer J, Norato DY, Shapiro E, Thomas J, Viskochil D, Wraith JE. Pastores GM, et al. Among authors: wraith je. Mol Genet Metab. 2007 May;91(1):37-47. doi: 10.1016/j.ymgme.2007.01.011. Epub 2007 Mar 2. Mol Genet Metab. 2007. PMID: 17336562

4

Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I.

Clarke LA, Wraith JE, Beck M, Kolodny EH, Pastores GM, Muenzer J, Rapoport DM, Berger KI, Sidman M, Kakkis ED, Cox GF. Clarke LA, et al. Among authors: wraith je. Pediatrics. 2009 Jan;123(1):229-40. doi: 10.1542/peds.2007-3847. Pediatrics. 2009. PMID: 19117887 Clinical Trial.

5

Enzyme replacement therapy for mucopolysaccharidosis VI: a phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study.

Harmatz P, Giugliani R, Schwartz I, Guffon N, Teles EL, Miranda MC, Wraith JE, Beck M, Arash L, Scarpa M, Yu ZF, Wittes J, Berger KI, Newman MS, Lowe AM, Kakkis E, Swiedler SJ; MPS VI Phase 3 Study Group. Harmatz P, et al. Among authors: wraith je. J Pediatr. 2006 Apr;148(4):533-539. doi: 10.1016/j.jpeds.2005.12.014. J Pediatr. 2006. PMID: 16647419 Clinical Trial.

6

Use of enzyme replacement therapy (Laronidase) before hematopoietic stem cell transplantation for mucopolysaccharidosis I: experience in 18 patients.

Wynn RF, Mercer J, Page J, Carr TF, Jones S, Wraith JE. Wynn RF, et al. Among authors: wraith je. J Pediatr. 2009 Jan;154(1):135-9. doi: 10.1016/j.jpeds.2008.07.004. J Pediatr. 2009. PMID: 19187736

7

Mucopolysaccharidosis type II (Hunter syndrome): a clinical review and recommendations for treatment in the era of enzyme replacement therapy.

Wraith JE, Scarpa M, Beck M, Bodamer OA, De Meirleir L, Guffon N, Meldgaard Lund A, Malm G, Van der Ploeg AT, Zeman J. Wraith JE, et al. Eur J Pediatr. 2008 Mar;167(3):267-77. doi: 10.1007/s00431-007-0635-4. Epub 2007 Nov 23. Eur J Pediatr. 2008. PMID: 18038146 Free PMC article. Review.

8

Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase).

Wraith JE, Beck M, Lane R, van der Ploeg A, Shapiro E, Xue Y, Kakkis ED, Guffon N. Wraith JE, et al. Pediatrics. 2007 Jul;120(1):e37-46. doi: 10.1542/peds.2006-2156. Epub 2007 Jun 4. Pediatrics. 2007. PMID: 17606547 Clinical Trial.

9

Enzyme replacement therapy with idursulfase in patients with mucopolysaccharidosis type II.

Wraith JE. Wraith JE. Acta Paediatr. 2008 Apr;97(457):76-8. doi: 10.1111/j.1651-2227.2008.00661.x. Acta Paediatr. 2008. PMID: 18339193 Review.

10

Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase.

Harmatz P, Yu ZF, Giugliani R, Schwartz IV, Guffon N, Teles EL, Miranda MC, Wraith JE, Beck M, Arash L, Scarpa M, Ketteridge D, Hopwood JJ, Plecko B, Steiner R, Whitley CB, Kaplan P, Swiedler SJ, Hardy K, Berger KI, Decker C. Harmatz P, et al. Among authors: wraith je. J Inherit Metab Dis. 2010 Feb;33(1):51-60. doi: 10.1007/s10545-009-9007-8. Epub 2010 Feb 6. J Inherit Metab Dis. 2010. PMID: 20140523 Free PMC article. Clinical Trial.

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