Design of phase III clinical trials for treatments of orphan retinal diseases: an overview of considerations

Retina. 2005 Dec;25(8 Suppl):S69-S71. doi: 10.1097/00006982-200512001-00033.
No abstract available

Publication types

  • Review

MeSH terms

  • Clinical Trials, Phase III as Topic / methods*
  • Eye Diseases, Hereditary / genetics
  • Eye Diseases, Hereditary / therapy*
  • Humans
  • Rare Diseases / genetics
  • Rare Diseases / therapy*
  • Research Design*
  • Retinal Diseases / genetics
  • Retinal Diseases / therapy*