A barrel of monkeys: scAAV8 gene therapy for hemophilia in nonhuman primates
Mol Ther
.
2011 May;19(5):826-7.
doi: 10.1038/mt.2011.73.
Authors
Randy J Chandler
1
,
Charles P Venditti
Affiliation
1
Organic Acid Research Section, Genetics and Molecular Biology Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland 20893, USA.
PMID:
21532610
PMCID:
PMC3098648
DOI:
10.1038/mt.2011.73
No abstract available
Publication types
Comment
MeSH terms
Animals
Capsid Proteins / metabolism*
Dependovirus / genetics*
Factor IX / metabolism*
Genetic Therapy / methods*
Hemophilia B / therapy*
Humans
Substances
Capsid Proteins
Factor IX
Grants and funding
Z01 HG200318-04/Intramural NIH HHS/United States
Z01 HG200318-05/Intramural NIH HHS/United States
Z99 HG999999/Intramural NIH HHS/United States