Trofinetide receives FDA approval as first drug for Rett syndrome.
Mughal ZUN, Ahmed B, Rangwala BS, Rangwala HS, Fatima H, Ali M, Farah AA.
Mughal ZUN, et al. Among authors: rangwala hs.
Ann Med Surg (Lond). 2024 Mar 18;86(5):2382-2385. doi: 10.1097/MS9.0000000000001896. eCollection 2024 May.
Ann Med Surg (Lond). 2024.
PMID: 38694380
Free PMC article.
No abstract available.