A novel small molecule target in human airway smooth muscle for potential treatment of obstructive lung diseases: a staged high-throughput biophysical screening

Respir Res. 2011 Jan 13;12(1):8. doi: 10.1186/1465-9921-12-8.

Abstract

Background: A newly identified mechanism of smooth muscle relaxation is the interaction between the small heat shock protein 20 (HSP20) and 14-3-3 proteins. Focusing upon this class of interactions, we describe here a novel drug target screening approach for treating airflow obstruction in asthma.

Methods: Using a high-throughput fluorescence polarization (FP) assay, we screened a library of compounds that could act as small molecule modulators of HSP20 signals. We then applied two quantitative, cell-based biophysical methods to assess the functional efficacy of these molecules and rank-ordered their abilities to relax isolated human airway smooth muscle (ASM). Scaling up to the level of an intact tissue, we confirmed in a concentration-responsive manner the potency of the cell-based hit compounds.

Results: Among 58,019 compound tested, 268 compounds caused 20% or more reduction of the polarized emission in the FP assay. A small subset of these primary screen hits, belonging to two scaffolds, caused relaxation of isolated ASM cell in vitro and attenuated active force development of intact tissue ex vivo.

Conclusions: This staged biophysical screening paradigm provides proof-of-principle for high-throughput and cost-effective discovery of new small molecule therapeutic agents for obstructive lung diseases.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • 14-3-3 Proteins / metabolism*
  • Animals
  • Bronchodilator Agents / chemistry
  • Bronchodilator Agents / pharmacology*
  • Cattle
  • Dose-Response Relationship, Drug
  • Drug Discovery / methods*
  • Fluorescence Polarization
  • Fourier Analysis
  • HSP20 Heat-Shock Proteins / metabolism*
  • High-Throughput Screening Assays
  • Humans
  • In Vitro Techniques
  • Lung / drug effects*
  • Lung / metabolism
  • Lung Diseases, Obstructive / drug therapy*
  • Lung Diseases, Obstructive / metabolism
  • Magnetics
  • Male
  • Molecular Structure
  • Muscle Relaxation / drug effects*
  • Muscle, Smooth / drug effects*
  • Muscle, Smooth / metabolism
  • Phosphorylation
  • Rats
  • Rats, Inbred F344
  • Reproducibility of Results
  • Signal Transduction / drug effects
  • Small Molecule Libraries
  • Structure-Activity Relationship
  • Surface Plasmon Resonance
  • Time Factors

Substances

  • 14-3-3 Proteins
  • Bronchodilator Agents
  • HSP20 Heat-Shock Proteins
  • Small Molecule Libraries