Management of primary vasculitides with biologic and novel small molecule medications

Curr Opin Rheumatol. 2021 Jan;33(1):8-14. doi: 10.1097/BOR.0000000000000756.

Abstract

Purpose of review: Vasculitides can affect small, medium and/or large vessels, leading to end-organ damage, decreased quality of life and death. Glucocorticoids remain the backbone of treatment for systemic vasculitis but are associated with numerous toxicities. In recent years, the efficacy of glucocorticoid-sparing biologic and novel small molecule therapies has been demonstrated.

Recent findings: In giant cell arteritis, tocilizumab was superior to glucocorticoid monotherapy in maintenance remission and cumulative glucocorticoid exposure and is now approved for the treatment of giant cell arteritis. In addition to the previously demonstrated efficacy of rituximab for remission induction in antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis, recent trials have also demonstrated its superiority for remission maintenance compared to alternative approaches. Mepolizumab is superior to standard of care alone with regard to remission rates and glucocorticoid-sparing effect in refractory eosinophilic granulomatosis with polyangiitis. Avacopan has shown significant promise in ANCA-associated vasculitis as part of a glucocorticoid-free induction regimen in a recently completed phase 3 trial. Use of biologics in rarer vasculitides remains guided by reports from small case series.

Summary: Biologics and other novel therapies have an increasingly important role in the management of systemic vasculitis. Additional studies are needed to define their optimal use and to guide their use in more rare forms of vasculitis.

Trial registration: ClinicalTrials.gov NCT02198248 NCT04157348 NCT03967925 NCT03712345.

Publication types

  • Research Support, N.I.H., Extramural
  • Review

MeSH terms

  • Aniline Compounds / therapeutic use
  • Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis / drug therapy
  • Antibodies, Antineutrophil Cytoplasmic / metabolism
  • Antibodies, Monoclonal, Humanized / therapeutic use
  • Autoimmune Diseases / drug therapy
  • Biological Products / therapeutic use*
  • Churg-Strauss Syndrome / drug therapy
  • Giant Cell Arteritis / drug therapy
  • Glucocorticoids / therapeutic use
  • Granulomatosis with Polyangiitis / drug therapy
  • Humans
  • Immunosuppressive Agents / therapeutic use
  • Nipecotic Acids / therapeutic use
  • Quality of Life
  • Remission Induction
  • Rituximab / therapeutic use
  • Vasculitis / drug therapy*

Substances

  • Aniline Compounds
  • Antibodies, Antineutrophil Cytoplasmic
  • Antibodies, Monoclonal, Humanized
  • Biological Products
  • Glucocorticoids
  • Immunosuppressive Agents
  • Nipecotic Acids
  • Rituximab
  • mepolizumab
  • tocilizumab
  • avacopan

Associated data

  • ClinicalTrials.gov/NCT02198248
  • ClinicalTrials.gov/NCT04157348
  • ClinicalTrials.gov/NCT03967925
  • ClinicalTrials.gov/NCT03712345