Low-dose non-steroidal anti-inflammatory drugs: a promising approach for the treatment of symptomatic bone marrow failure in Ghosal hematodiaphyseal dysplasia
Haematologica. 2024 Mar 14.
doi: 10.3324/haematol.2023.284098.
Online ahead of print.
1 Department of Hematology and Bone Marrow Transplantation, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris. jonathan.bordat@aphp.fr.
2 Paris Cité University, Paris, France; Imagine Institute, INSERM UMR 1163, Laboratory of Molecular Mechanisms of Hematologic Disorders and Therapeutic Implications, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; Adult Hematology, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
3 Paris Cité University, Paris, France; French Reference Center for Skeletal Dysplasia, INSERM UMR 1163, Imagine Institute, Necker Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
4 Department of Hematology and Bone Marrow Transplantation, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; Paris Cité University, Paris, France; French Reference Center for Aplastic Anemia, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
5 Paris Cité University, Paris, France; French Reference Center for Aplastic Anemia, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; Laboratory of Hematology, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
6 Department of Pathology, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
7 French Reference Center for Skeletal Dysplasia, INSERM UMR 1163, Imagine Institute, Necker Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris.
8 Hemophilia Treatment Centre, University Hospital of Réunion, Réunion Island.
9 Department of Hematology and Bone Marrow Transplantation, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; French Reference Center for Aplastic Anemia, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris. flore.sicre-de-fontbrune@aphp.fr.