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Fetal gene therapy for neurodegenerative disease of infants.
Massaro G, Mattar CNZ, Wong AMS, Sirka E, Buckley SMK, Herbert BR, Karlsson S, Perocheau DP, Burke D, Heales S, Richard-Londt A, Brandner S, Huebecker M, Priestman DA, Platt FM, Mills K, Biswas A, Cooper JD, Chan JKY, Cheng SH, Waddington SN, Rahim AA. Massaro G, et al. Among authors: chan jky. Nat Med. 2018 Sep;24(9):1317-1323. doi: 10.1038/s41591-018-0106-7. Epub 2018 Jul 16. Nat Med. 2018. PMID: 30013199 Free PMC article.
In utero gene transfer to the mouse nervous system.
Rahim AA, Wong AM, Buckley SM, Chan JK, David AL, Cooper JD, Coutelle C, Peebles DM, Waddington SN. Rahim AA, et al. Biochem Soc Trans. 2010 Dec;38(6):1489-93. doi: 10.1042/BST0381489. Biochem Soc Trans. 2010. PMID: 21118113 Review.
Fetal gene therapy: recent advances and current challenges.
Mattar CN, Choolani M, Biswas A, Waddington SN, Chan JK. Mattar CN, et al. Expert Opin Biol Ther. 2011 Oct;11(10):1257-71. doi: 10.1517/14712598.2011.585153. Epub 2011 May 31. Expert Opin Biol Ther. 2011. PMID: 21623703 Review.
Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques.
Mattar CN, Nathwani AC, Waddington SN, Dighe N, Kaeppel C, Nowrouzi A, Mcintosh J, Johana NB, Ogden B, Fisk NM, Davidoff AM, David A, Peebles D, Valentine MB, Appelt JU, von Kalle C, Schmidt M, Biswas A, Choolani M, Chan JK. Mattar CN, et al. Mol Ther. 2011 Nov;19(11):1950-60. doi: 10.1038/mt.2011.107. Epub 2011 May 31. Mol Ther. 2011. PMID: 21629224 Free PMC article.
Perinatal gene transfer to the liver.
McKay TR, Rahim AA, Buckley SM, Ward NJ, Chan JK, Howe SJ, Waddington SN. McKay TR, et al. Curr Pharm Des. 2011;17(24):2528-41. doi: 10.2174/138161211797247541. Curr Pharm Des. 2011. PMID: 21774770 Free PMC article. Review.
290 results