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CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
Frangoul H, Altshuler D, Cappellini MD, Chen YS, Domm J, Eustace BK, Foell J, de la Fuente J, Grupp S, Handgretinger R, Ho TW, Kattamis A, Kernytsky A, Lekstrom-Himes J, Li AM, Locatelli F, Mapara MY, de Montalembert M, Rondelli D, Sharma A, Sheth S, Soni S, Steinberg MH, Wall D, Yen A, Corbacioglu S. Frangoul H, et al. Among authors: handgretinger r. N Engl J Med. 2021 Jan 21;384(3):252-260. doi: 10.1056/NEJMoa2031054. Epub 2020 Dec 5. N Engl J Med. 2021. PMID: 33283989 Clinical Trial.
Will post-transplantation cell therapies for pediatric patients become standard of care?
Lankester AC, Locatelli F, Bader P, Rettinger E, Egeler M, Katewa S, Pulsipher MA, Nierkens S, Schultz K, Handgretinger R, Grupp SA, Boelens JJ, Bollard CM; Westhafen Intercontinental Group. Lankester AC, et al. Among authors: handgretinger r. Biol Blood Marrow Transplant. 2015 Mar;21(3):402-11. doi: 10.1016/j.bbmt.2014.07.018. Epub 2014 Jul 23. Biol Blood Marrow Transplant. 2015. PMID: 25064748 Free article. Review.
Comparative targeting analysis of KLF1, BCL11A, and HBG1/2 in CD34+ HSPCs by CRISPR/Cas9 for the induction of fetal hemoglobin.
Lamsfus-Calle A, Daniel-Moreno A, Antony JS, Epting T, Heumos L, Baskaran P, Admard J, Casadei N, Latifi N, Siegmund DM, Kormann MSD, Handgretinger R, Mezger M. Lamsfus-Calle A, et al. Among authors: handgretinger r. Sci Rep. 2020 Jun 23;10(1):10133. doi: 10.1038/s41598-020-66309-x. Sci Rep. 2020. PMID: 32576837 Free PMC article.
Blinatumomab in pediatric patients with relapsed/refractory acute lymphoblastic leukemia: results of the RIALTO trial, an expanded access study.
Locatelli F, Zugmaier G, Mergen N, Bader P, Jeha S, Schlegel PG, Bourquin JP, Handgretinger R, Brethon B, Rossig C, Chen-Santel C. Locatelli F, et al. Among authors: handgretinger r. Blood Cancer J. 2020 Jul 24;10(7):77. doi: 10.1038/s41408-020-00342-x. Blood Cancer J. 2020. PMID: 32709851 Free PMC article. No abstract available.
544 results