Multimodal mechanisms of pathogenic variants in the signal peptide of FIX leading to hemophilia B.
Gao M, Chen L, Yang J, Dong S, Cao Q, Cui Z, Dong Y, Liu H, Shen Y, Yang H, Hao Z, Zhang L, Li W, Tie JK, Shen GM.
Gao M, et al. Among authors: li w.
Blood Adv. 2024 May 31:bloodadvances.2023012432. doi: 10.1182/bloodadvances.2023012432. Online ahead of print.
Blood Adv. 2024.
PMID: 38820490