Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1-Year Interim Results from Study SRP-9001-103 (ENDEAVOR).
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Zaidman CM, et al. Among authors: murphy ap.
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Ann Neurol. 2023.
PMID: 37539981