Small-molecule eRF3a degraders rescue CFTR nonsense mutations by promoting premature termination codon readthrough.
Lee RE, Lewis CA, He L, Bulik-Sullivan EC, Gallant SC, Mascenik TM, Dang H, Cholon DM, Gentzsch M, Morton LC, Minges JT, Theile JW, Castle NA, Knowles MR, Kimple AJ, Randell SH.
Lee RE, et al. Among authors: minges jt.
J Clin Invest. 2022 Sep 15;132(18):e154571. doi: 10.1172/JCI154571.
J Clin Invest. 2022.
PMID: 35900863
Free PMC article.