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Pediatric Bone Marrow Failure: A Broad Landscape in Need of Personalized Management.
J Clin Med. 2023 Nov 20;12(22):7185. doi: 10.3390/jcm12227185.
J Clin Med. 2023.
PMID: 38002797
Free PMC article.
Review.
Optimizing diagnostic methods and stem cell transplantation outcomes in pediatric bone marrow failure: a 50-year single center experience.
Vissers L, van der Burg M, Lankester A, Smiers F, Mohseny A.
Vissers L, et al.
Eur J Pediatr. 2023 Sep;182(9):4195-4203. doi: 10.1007/s00431-023-05093-y. Epub 2023 Jul 13.
Eur J Pediatr. 2023.
PMID: 37439851
Free PMC article.
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Second Tier Testing to Reduce the Number of Non-actionable Secondary Findings and False-Positive Referrals in Newborn Screening for Severe Combined Immunodeficiency.
Blom M, Pico-Knijnenburg I, Imholz S, Vissers L, Schulze J, Werner J, Bredius R, van der Burg M.
Blom M, et al.
J Clin Immunol. 2021 Nov;41(8):1762-1773. doi: 10.1007/s10875-021-01107-2. Epub 2021 Aug 9.
J Clin Immunol. 2021.
PMID: 34370170
Free PMC article.
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