Ethical Challenges Confronted When Providing Nusinersen Treatment for Spinal Muscular Atrophy.
Burgart AM, Magnus D, Tabor HK, Paquette ED, Frader J, Glover JJ, Jackson BM, Harrison CH, Urion DK, Graham RJ, Brandsema JF, Feudtner C.
Burgart AM, et al. Among authors: jackson bm.
JAMA Pediatr. 2018 Feb 1;172(2):188-192. doi: 10.1001/jamapediatrics.2017.4409.
JAMA Pediatr. 2018.
PMID: 29228163