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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1997 1
2000 1
2003 1
2004 1
2009 1
2010 1
2011 2
2012 2
2013 3
2014 4
2015 3
2016 3
2017 1
2018 7
2019 4
2020 2
2022 4
2023 10
2024 1

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47 results

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Page 1
Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy.
Birch SM, Lawlor MW, Conlon TJ, Guo LJ, Crudele JM, Hawkins EC, Nghiem PP, Ahn M, Meng H, Beatka MJ, Fickau BA, Prieto JC, Styner MA, Struharik MJ, Shanks C, Brown KJ, Golebiowski D, Bettis AK, Balog-Alvarez CJ, Clement N, Coleman KE, Corti M, Pan X, Hauschka SD, Gonzalez JP, Morris CA, Schneider JS, Duan D, Chamberlain JS, Byrne BJ, Kornegay JN. Birch SM, et al. Sci Transl Med. 2023 Jan 4;15(677):eabo1815. doi: 10.1126/scitranslmed.abo1815. Epub 2023 Jan 4. Sci Transl Med. 2023. PMID: 36599002 Free PMC article.
Viral vector-mediated gene therapies.
Hollinger K, Chamberlain JS. Hollinger K, et al. Curr Opin Neurol. 2015 Oct;28(5):522-7. doi: 10.1097/WCO.0000000000000241. Curr Opin Neurol. 2015. PMID: 26263476 Free PMC article. Review.
Efficacy and muscle safety assessment of fukutin-related protein gene therapy.
Benasutti H, Maricelli JW, Seto J, Hall J, Halbert C, Wicki J, Heusgen L, Purvis N, Regnier M, Lin DC, Rodgers BD, Chamberlain JS. Benasutti H, et al. Mol Ther Methods Clin Dev. 2023 Jun 4;30:65-80. doi: 10.1016/j.omtm.2023.05.022. eCollection 2023 Sep 14. Mol Ther Methods Clin Dev. 2023. PMID: 37361354 Free PMC article.
A Boost for Muscle with Gene Therapy.
Chamberlain JS. Chamberlain JS. N Engl J Med. 2022 Mar 24;386(12):1184-1186. doi: 10.1056/NEJMcibr2118576. N Engl J Med. 2022. PMID: 35320650 No abstract available.
Clinical potential of microdystrophin as a surrogate endpoint.
Boehler JF, Brown KJ, Beatka M, Gonzalez JP, Donisa Dreghici R, Soustek-Kramer M, McGonigle S, Ganot A, Palmer T, Lowie C, Chamberlain JS, Lawlor MW, Morris CA. Boehler JF, et al. Neuromuscul Disord. 2023 Jan;33(1):40-49. doi: 10.1016/j.nmd.2022.12.007. Epub 2022 Dec 14. Neuromuscul Disord. 2023. PMID: 36575103 Free article. Review.
47 results