Hematopoietic stem-cell transplantation in globoid-cell leukodystrophy.
Krivit W, Shapiro EG, Peters C, Wagner JE, Cornu G, Kurtzberg J, Wenger DA, Kolodny EH, Vanier MT, Loes DJ, Dusenbery K, Lockman LA.
Krivit W, et al.
N Engl J Med. 1998 Apr 16;338(16):1119-26. doi: 10.1056/NEJM199804163381605.
N Engl J Med. 1998.
PMID: 9545360
Free article.
Clinical Trial.