Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-linked adrenoleukodystrophy.
Shapiro E, Krivit W, Lockman L, Jambaqué I, Peters C, Cowan M, Harris R, Blanche S, Bordigoni P, Loes D, Ziegler R, Crittenden M, Ris D, Berg B, Cox C, Moser H, Fischer A, Aubourg P.
Shapiro E, et al.
Lancet. 2000 Aug 26;356(9231):713-8. doi: 10.1016/S0140-6736(00)02629-5.
Lancet. 2000.
PMID: 11085690