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Depletion of SMN protein in mesenchymal progenitors impairs the development of bone and neuromuscular junction in spinal muscular atrophy.
Elife. 2024 Feb 6;12:RP92731. doi: 10.7554/eLife.92731.
Elife. 2024.
PMID: 38318851
Free PMC article.
Improved therapeutic approach for spinal muscular atrophy via ubiquitination-resistant survival motor neuron variant.
Rhee J, Kang JS, Jo YW, Yoo K, Kim YL, Hann SH, Kim YE, Kim H, Kim JH, Kong YY.
Rhee J, et al.
J Cachexia Sarcopenia Muscle. 2024 Apr 22. doi: 10.1002/jcsm.13486. Online ahead of print.
J Cachexia Sarcopenia Muscle. 2024.
PMID: 38650097
Free article.
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